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Phase 3 N=148 Randomized Treatment

A Study of Donanemab (LY3002813) Compared With Aducanumab in Participants With Early Symptomatic Alzheimer's Disease (TRAILBLAZER-ALZ 4)

Mild Cognitive Impairment (MCI) · Alzheimer Disease

Enrolled (actual)
148
Serious AEs
15.0%
Results posted
Nov 2023
Primary outcome: Primary: Percentage of Participants Who Reach Complete Amyloid Plaque Clearance on Florbetapir F18 Positron Emission Tomography (PET) Scan (Superiority) on Donanemab Versus Aducanumab — 1.6; 37.9 Percentage of participants — p=<0.001

Study Design & Population

Study type
Interventional
Phase
Phase 3
Interventions
Donanemab (Drug); Aducanumab (Drug)
Age
Adult, Older Adult · 50+ yrs
Sex
All
Sponsor
Eli Lilly and Company
Primary completion
Sep 2022

Outcome Measures

OutcomeResultp-value
PRIMARY
Percentage of Participants Who Reach Complete Amyloid Plaque Clearance on Florbetapir F18 Positron Emission Tomography (PET) Scan (Superiority) on Donanemab Versus Aducanumab
43.10; 76.79 <0.001 sig
PRIMARY
Percentage of Participants Who Reach Complete Amyloid Plaque Clearance on Florbetapir F18 PET Scan in the Low/Medium (Intermediate) Subpopulation (Superiority) on Donanemab Versus Aducanumab
43.48; 72.00 0.022 sig
SECONDARY
Mean Absolute Change From Baseline in Brain Amyloid Plaque on Florbetapir F18 PET Scan (Superiority) on Donanemab Versus Aducanumab
-72.18; -84.22 0.004 sig
SECONDARY
Mean Percent Change From Baseline in Brain Amyloid Plaque on Florbetapir F18 PET Scan (Superiority) Donanemab Versus Aducanumab
-72.84; -86.29 0.002 sig
SECONDARY
Change From Baseline in Brain Amyloid Plaque on Florbetapir F18 PET Scan in the Low/Medium (Intermediate) Tau Subpopulation (Superiority) on Donanemab Versus Aducanumab
-23.824; -64.076 <0.001 sig
SECONDARY
Mean Absolute Change From Baseline in Brain Amyloid Plaque on Florbetapir F18 PET Scan (Superiority) on Donanemab Versus Aducanumab
-72.18; -84.22 0.004 sig
SECONDARY
Mean Percent Change From Baseline in Brain Amyloid Plaque on Florbetapir F18 PET Scan (Superiority) Donanemab Versus Aducanumab
-72.84; -86.29 0.002 sig
SECONDARY
Percentage of Participants Who Reach Complete Amyloid Plaque Clearance on Florbetapir F18 Positron Emission Tomography (PET) Scan (Superiority) on Donanemab Versus Aducanumab
43.10; 76.79 <0.001 sig
SECONDARY
Percentage of Participants Who Reach Complete Amyloid Plaque Clearance on Florbetapir F18 PET Scan in the Low/Medium (Intermediate) Subpopulation (Superiority) on Donanemab Versus Aducanumab
43.48; 72.00 0.022 sig
SECONDARY
Mean Absolute Change From Baseline in Brain Amyloid Plaque on Florbetapir F18 PET Scan in the Low/Medium (Intermediate) Tau Subpopulation (Superiority) on Donanemab Versus Aducanumab
-72.24; -86.57 0.028 sig
SECONDARY
Mean Absolute Change From Baseline in Brain Amyloid Plaque on Florbetapir F18 PET Scan (Superiority) on Donanemab 6 Months Versus Aducanumab 12 Months
-56.056; -63.987 0.0558
SECONDARY
Mean Absolute Change From Baseline in Brain Amyloid Plaque on Florbetapir F18 PET Scan (Non-inferiority) on Donanemab 6 Months Versus Aducanumab 12 Months
-56.056; -63.987
SECONDARY
Mean Absolute Change From Baseline in Brain Amyloid Plaque on Florbetapir F18 PET Scan (Superiority) on Donanemab Versus Aducanumab
-72.18; -84.22 0.004 sig
SECONDARY
Time to Reach Complete Amyloid Plaque Clearance on Donanemab Versus Aducanumab
568.00; 359.00 <0.001 sig
SECONDARY
Mean Percent Change From Baseline in Brain Amyloid Plaque on Florbetapir F18 PET Scan (Superiority) Donanemab Versus Aducanumab
-72.84; -86.29 0.002 sig
SECONDARY
Percentage of Participants Who Reach Complete Amyloid Plaque Clearance on Florbetapir F18 Positron Emission Tomography (PET) Scan (Superiority) on Donanemab Versus Aducanumab
43.10; 76.79 <0.001 sig
SECONDARY
Percentage of Participants Who Reach Complete Amyloid Plaque Clearance on Florbetapir F18 PET Scan in the Low/Medium (Intermediate) Subpopulation (Superiority) on Donanemab Versus Aducanumab
43.48; 72.00 0.022 sig
SECONDARY
Mean Absolute Change From Baseline in Brain Amyloid Plaque on Florbetapir F18 PET Scan in the Low/Medium (Intermediate) Tau Subpopulation (Superiority) on Donanemab Versus Aducanumab
-72.24; -86.57 0.028 sig
SECONDARY
Mean Absolute Change From Baseline in Brain Amyloid Plaque on Florbetapir F18 PET Scan (Non-inferiority) on Donanemab 6 Months Versus Aducanumab 18 Months
-72.178; -64.347

Summary

The main purpose of this study is to compare donanemab to aducanumab on brain amyloid plaque clearance in participants with early symptomatic Alzheimer's Disease (AD).

Eligibility Criteria

Inclusion Criteria

  • Gradual and progressive change in memory function reported by the participant or informant for ≥6 months.
  • Meet florbetapir F18 PET scan criteria.
  • A Clinical Dementia Rating (CDR)-Global Score of 0.5 or 1.
  • Must consent to apolipoprotein E (ApoE) genotyping
  • Must have a mini mental state examination (MMSE) score between 20 and 30
  • Have a study partner who will provide written informed consent to participate, is in frequent contact with the participant (defined as at least 10 hours per week), and will accompany the participant to study visits or be available by telephone at designated times.
  • Have adequate literacy, vision, and hearing for neuropsychological testing in the opinion of the investigator at the time of screening.
  • Women not of childbearing potential may participate

Exclusion Criteria

  • Significant neurological disease affecting the central nervous system (other than AD), that may affect cognition or ability to complete the study, including but not limited to, other dementias, serious infection of the brain, Parkinson's disease, multiple concussions, history of transient ischemic attack or stroke, or epilepsy or recurrent seizures (except febrile childhood seizures).
  • Current serious or unstable medical illnesses including cardiovascular, hepatic, renal, gastroenterologic, respiratory, endocrinologic, psychiatric (including actively suicidal or deemed at risk of suicide, or current alcohol or substance abuse), immunologic, infectious, or hematologic disease and other conditions that, in the investigator's opinion, could interfere with the analyses in this study; or has a life expectancy of approximately

≤24 months.

  • History of clinically significant multiple or severe drug allergies, or severe posttreatment hypersensitivity reactions (including but not limited to erythema multiforme major, linear immunoglobulin A dermatosis, toxic epidermal necrolysis, and/or exfoliative dermatitis).
  • History of bleeding disorder or use of medications with platelet anti-aggregant or anti-coagulant properties (unless aspirin at ≤325 milligram (mg).
  • Have had prior or current treatment with donanemab or aducanumab
  • Have known allergies to donanemab or aducanumab, related compounds, or any components of the formulation
  • Prior or current participation in any immunotherapy study targeting Amyloid beta
View full record on ClinicalTrials.gov →

Data sourced from ClinicalTrials.gov (NCT05108922). Outcome figures and adverse-event rates are extracted automatically from the registry's posted results and are provided for clinician reference, not as a substitute for the primary publication.

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