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Clinical Trial Search

Completed trials with posted results — search by concept, filter by the parameters that matter at the bedside.

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30 closest matches · ranked by relevance

Phase 3 N=238 Study of Ataluren (PTC124™) in Cystic Fibrosis

Cystic Fibrosis
Primary: Percentage of Predicted Function (Percent-Predicted) of Forced Expiratory Volume in One Second (FEV1) at Baseline — 62.092; 60.232 percentage of predicted FEV1 — p=0.3264
PTC Therapeutics Results May 2020 40.3% serious AE View details

N/A N=314 Primary Immunodeficiency in Kuwait

Primary Immune Deficiency Disorder
Primary: Number of Participants With Different Epidemiological Features — 287; 100; 68; 56 patients
Kuwait Society for Allergy and Clinical Immunology Results Sep 2019 View details

Phase 3 N=12 Betaine and Peroxisome Biogenesis Disorders

Peroxisome Biogenesis Disorders
Primary: Peroxisome Biochemical Functions as Measured by Plasma Very Long Chain Fatty Acid — 0.180; 0.188 ratio
McGill University Health Centre/Research… Results Jun 2016 0.0% serious AE View details