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Phase 2 N=1 Treatment

Effects of Leptin Replacement in Children

Obesity · Metabolic Syndrome · Diabetes

Enrolled (actual)
1
Serious AEs
Results posted
Feb 2020
Primary outcome: Primary: Weight — NA lbs

Study Design & Population

Study type
Interventional
Phase
Phase 2
Interventions
Recombinant methionyl human leptin (Drug)
Age
Pediatric, Adult · 5+ yrs
Sex
Male
Sponsor
University of Miami
Primary completion
Apr 2010

Outcome Measures

OutcomeResultp-value
PRIMARY
Weight
NA
SECONDARY
Glucose Levels
NA
SECONDARY
Bone Mineral Density
NA

Summary

To assess the endocrine and immune effects of leptin replacement in leptin-deficient children, from a consanguineous family. The hypothesis is that leptin replacement will have significant effects on endocrine function.

Eligibility Criteria

Inclusion Criteria

  • Children with a functional leptin gene mutation from a consanguineous Turkish family. Only one leptin-naïve child from this family is alive and eligible.

Exclusion Criteria

  • N/A
View full record on ClinicalTrials.gov →

Data sourced from ClinicalTrials.gov (NCT00659828). Outcome figures and adverse-event rates are extracted automatically from the registry's posted results and are provided for clinician reference, not as a substitute for the primary publication.

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