How many clinical trials are tracked of ataluren?

14 trials are tracked, 4 with published results.

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ataluren

1 published article · Updated continuously

Clinical Trial Landscape

Clinical Trials of ataluren

14 trials tracked of ataluren: 6 in phase 3 or 4 and 4 with published results. The most-cited published study has 454 citations.

14Trials tracked

6Phase 3 & 4

0Recruiting

4With published results

Phase distribution

Phase 4 1 Phase 3 5 Phase 2 8

Phase 3 Phase 3 Study of Ataluren in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) Completed · 454 cited
Phase 3 Study of Ataluren (PTC124™) in Cystic Fibrosis Completed · 335 cited
Phase 3 Study of Ataluren for Previously Treated Participants With Nonsense Mutation Duchenne/Becker Muscular Dystrophy (nmDBMD) in Europe, Israel, Australia, and Canada Completed · 62 cited
Phase 3 Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophy Completed
Phase 4 PTC Study to Evaluate Ataluren in Combination With Ivacaftor Completed
Phase 3 Extension Study of Ataluren (PTC124) in Cystic Fibrosis Completed

Show 8 more trials

Phase 2 A Study of Ataluren in Pediatric Participants With Cystic Fibrosis Completed
Phase 2 Study of Ataluren in ≥2 to <5 Year-Old Male Participants With Duchenne Muscular Dystrophy Completed
Phase 2 A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) Who Have Been Treated With Ataluren Completed
Phase 2 Ataluren for Nonsense Mutation in CDKL5 and Dravet Syndrome Completed
Phase 2 A Study to Evaluate the Safety and Pharmacokinetics of Ataluren in Participants From ≥6 Months to <2 Years of Age With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) Completed
Phase 2 A Study to Assess Dystrophin Levels in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD) Completed
Phase 2 Study of Ataluren in Participants With Nonsense Mutation Aniridia Completed
Phase 2 Phase 2B Study of PTC124 (Ataluren) in Duchenne/Becker Muscular Dystrophy (DMD/BMD) Completed

Showing the 14 most-cited and recently-updated of 14 trials. Browse the full registry →

Trial data sourced from ClinicalTrials.gov. Counts describe the research landscape and are not a treatment recommendation. Informational only — not medical advice.