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Home › Medications › idebenone

idebenone

2 published articles · Updated continuously

Clinical Trial Landscape

Clinical Trials of idebenone

12 trials tracked of idebenone: 7 in phase 3 or 4 and 1 with published results. The most-cited published study has 48 citations.

12Trials tracked
7Phase 3 & 4
0Recruiting
1With published results
Phase distribution
Phase 4 1 Phase 3 6 Phase 2 5
  1. Phase 4 Study to Assess the Efficacy and Safety of Raxone in LHON Patients Completed · 48 cited
  2. Phase 3 A Study of Efficacy, Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia (FRDA) Patients Completed
  3. Phase 3 Long-Term Safety and Tolerability of Idebenone in Friedreich's Ataxia Patients (MICONOS Extension) Completed
  4. Phase 3 Patient Reported Outcomes in Friedreich's Ataxia Patients After Withdrawal From Treatment With Idebenone (PROTI) Completed
  5. Phase 3 Phase III Study of Idebenone in Duchenne Muscular Dystrophy (DMD) Completed
  6. Phase 3 Study to Assess the Efficacy, Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia Completed
Show 6 more trials
  1. Phase 3 Study to Assess the Safety and Tolerability of Idebenone in the Treatment of Friedreich's Ataxia Patients Completed
  2. Phase 2 Clinical Trial of Idebenone in Primary Progressive Multiple Sclerosis (IPPoMS) Completed
  3. Phase 2 Efficacy and Tolerability of Idebenone in Boys With Cardiac Dysfunction Associated With Duchenne Muscular Dystrophy Completed
  4. Phase 2 Idebenone for Primary Progressive Multiple Sclerosis Completed
  5. Phase 2 Study of Oral Idebenone to Treat Non-Alcoholic Steatohepatitis Completed
  6. Phase 2 Study of Idebenone in the Treatment of Mitochondrial Encephalopathy Lactic Acidosis & Stroke-like Episodes Completed

Showing the 12 most-cited and recently-updated of 12 trials. Browse the full registry →

Trial data sourced from ClinicalTrials.gov. Counts describe the research landscape and are not a treatment recommendation. Informational only — not medical advice.

HCP Mode — summaries include clinical detail, trial data, and statistical outcomes.
Patient Mode — summaries use plain language, avoiding clinical jargon.
Cochrane review finds uncertain benefits of drugs for Friedreich ataxia with low-certainty evidence
Cardiology Sys. Review
Cochrane review finds uncertain benefits of drugs for Friedreich ataxia with low-certainty evidence Cochrane review finds little benefit for drugs treating Friedreich ataxia
This Cochrane systematic review evaluated pharmacological treatments for people with genetically-confirmed Friedreich ataxia. The analysis i…
A major review of eight studies found that most drugs for Friedreich ataxia likely make little difference to key symptoms compared to placeb…
Cochrane May 16, 2026
Phase 1/2a trial tests oral idebenone safety in adults with NASH and fibrosis
Gastroenterology Phase II
Phase 1/2a trial tests oral idebenone safety in adults with NASH and fibrosis Can an oral drug help people with fatty liver disease? Early safety study begins
A randomized, double-blinded, placebo-controlled, single-center phase 1/2a study enrolled 53 adults with NASH and stage 1-3 fibrosis to asse…
A new oral drug for fatty liver disease has finished its early safety study, with results expected soon to show if it helps stop scarring.
CT.gov Mar 30, 2026