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Home › Conditions › achondroplasia

Achondroplasia

Part of Osteochondrodysplasias

1 published article · Updated continuously

Clinical Trial Landscape

Clinical Trials for achondroplasia

5 trials tracked for achondroplasia: 1 in phase 3 or 4 and 1 with published results. The most-cited published study has 19 citations.

5Trials tracked
1Phase 3 & 4
0Recruiting
1With published results
Phase distribution
Phase 3 1 Phase 2 3 Other / NA 1
  1. Phase 3 A Study to Evaluate the Efficacy and Safety of BMN 111 in Children With Achondroplasia Completed · 19 cited
  2. Phase 2 A Dose Escalation Trial Evaluating Safety, Efficacy, and Pharmacokinetics of TransCon CNP Administered Once Weekly in Prepubertal Children With Achondroplasia Completed
  3. Phase 2 A Clinical Trial to Evaluate the Safety and Efficacy of BMN 111 in Infants and Young Children With Achondroplasia Completed
  4. Phase 2 A Phase 2 Study of BMN 111 to Evaluate Safety, Tolerability, and Efficacy in Children With Achondroplasia Completed
  5. N/A A Study to Learn About Recifercept in Patients With Achondroplasia Completed

Showing the 5 most-cited and recently-updated of 5 trials. Browse the full registry →

Trial data sourced from ClinicalTrials.gov. Counts describe the research landscape and are not a treatment recommendation. Informational only — not medical advice.

HCP Mode — summaries include clinical detail, trial data, and statistical outcomes.
Patient Mode — summaries use plain language, avoiding clinical jargon.
Systematic review and meta-analysis of vosoritide in children with achondroplasia shows growth gains and injection site reactions
Pediatrics Meta-analysis
Systematic review and meta-analysis of vosoritide in children with achondroplasia shows growth gains and injection site reactions New Treatment Linked to Faster Growth in Children With Achondroplasia
This systematic review and single-arm meta-analysis evaluated vosoritide in children with genetically confirmed achondroplasia across 13 stu…
A new review shows a specific drug can help children with achondroplasia grow taller over one year.
Apr 24, 2026